
What is Gene Therapy? | FDA
Human gene therapy is the administration of genetic material to modify or manipulate the expression of a gene product or to alter the biological properties of living cells for therapeutic use.
Gene therapy - Wikipedia
Gene therapy is medical technology that aims to produce a therapeutic effect through the manipulation of gene expression or through altering the biological properties of living cells. …
Gene therapy - Mayo Clinic
Apr 23, 2024 · Gene therapy aims to fix a faulty gene or replace it with a healthy gene to try to cure disease or make the body better able to fight disease. It holds promise as a treatment for …
How does gene therapy work?: MedlinePlus Genetics
Gene therapy works by altering the genetic code to recover the functions of critical proteins. Proteins are the workhorses of the cell and the structural basis of the body’s tissues.
Gene Therapy - National Human Genome Research Institute
4 days ago · Gene therapy is a technique that uses a gene (s) to treat, prevent or cure a disease or medical disorder. Often, gene therapy works by adding new copies of a gene that is broken, …
Gene therapy | Description, Uses, Examples, & Safety Issues
3 days ago · Gene therapy, introduction of a normal gene into an individual’s genome in order to repair a mutation that causes a genetic disease. Human gene therapy has been attempted on …
What Is Gene Therapy? Pros, Cons & Examples - Cleveland Clinic
Jun 17, 2025 · Gene therapy is a way to treat some genetic diseases. It works by replacing a malfunctioning gene, “turning off” a disease-causing gene or giving you a new copy of a gene.
Gene therapy - Penn Medicine
What is gene therapy? Gene therapy is an emerging treatment option that utilizes the body’s genes to cure or fight disease. Treatments may involve repairing or replacing the body’s genes …
What Is Gene and Cell Therapy? | Mass General Brigham
Sep 3, 2025 · Gene therapy is designed to silence a mistake in the gene or replace the faulty gene with a corrected version. Usually, doctors use viruses to deliver the healthy, corrected …
What Is Gene Therapy: Risks, Benefits, and More - Verywell Health
Dec 11, 2025 · Learn about gene therapy, which attempts to cure disease or improve the body's ability to fight it by adding a new gene or replacing a faulty gene.